OpenNeedle Ask your own
The short version: the 2025 brain-targeted LNP study [29] measured transfection results, not particle routes, so it cannot rule out intact transcytosis.

The 2025 Science Advances study [29] engineered LNPs that, after intravenous injection, transfected about 10–13% of neurons, astrocytes, microglia, and brain capillary endothelial cells. That is a real finding. But it measured protein expression, the output of transfection. It did not label the LNP particles themselves and track whether intact particles appeared on the brain side of the BBB. Without that tracking experiment, the study cannot distinguish between two routes: intact LNPs crossing the BBB by transcytosis and then transfecting brain cells, versus LNPs being taken up by BBB endothelial cells, the mRNA being translated inside those cells, and the protein product being released into the brain. Both routes produce the same measured result.

The key experiment that would settle this is straightforward: inject fluorescently or radioactively labeled LNPs intravenously, then look for intact particles in brain tissue or cerebrospinal fluid using electron microscopy or fractionation, while also measuring whether the signal comes from intact particles or from degraded components. That experiment is not in this retrieval set. Without it, the claim that transcytosis does not happen is an inference from the absence of evidence, not a proven finding.

The other studies in this set do not fill the gap. A 2025 study that injected LNPs directly into the striatum [28] tells you nothing about crossing the BBB from the blood. A 2026 molecular dynamics study modeled LNP movement through brain extracellular matrix [25] but assumed the LNPs were already in the brain. The rest of the retrieval is about solid lipid nanoparticles for drug delivery [12, 15, 17, 24, 26, 27, 30, 31], BBB permeability in other contexts [1–9], or LNP biodistribution to liver and spleen [10, 11, 13, 14, 16, 19–22]. None of these studies designed an experiment to detect intact LNP transcytosis across the BBB.

My call: the evidence in this retrieval set does not rule out intact LNP transcytosis across the BBB. The claim that transfection of BBB cells is the only route is based on studies that did not test for transcytosis directly. Confidence: low.

Keep digging

Sources used 29

  1. An Integrating Sphere Based Method for Quantifying RNA Encapsulation Efficiency in Lipid Nanoparticles without Lysis Thin

    Develops a lysis-free, integrating-sphere method to quantify free and total RNA in intact lipid nanoparticles, enabling encapsulation efficiency calculation with results that agree with conventional RG assays and reduced lysis bias.

    DOI: 10.64898/2026.05.29.728751
  2. Antibody Targeted PET Imaging of 64 Cu-DOTA-Anti-CEA PEGylated Lipid Nanodiscs in CEA Positive Tumors Bioconjugate Chemistry (2020) Thin

    This study demonstrates that antibody-targeted lipid nanodiscs (LNDs) bearing 64Cu-DOTA can target CEA-expressing tumors in mice, with intact anti-CEA antibody conjugated LNDs achieving markedly higher tumor uptake than untargeted LNDs, while Fab' fragments offer limited improve…

    DOI: 10.1021/acs.bioconjchem.9b00854
  3. Development of Cell-Derived Plasma Membrane Vesicles as a Nanoparticle Encapsulation and Delivery System Cellular and Molecular Bioengineering (2025) Thin

    The study develops a vesicle-based loading approach to encapsulate silica nanoparticles inside cell membrane-derived giant plasma membrane vesicles (GPMVs) produced from A549 cells, yielding core-shell nanoparticle-GPMVs that can be taken up by recipient cells with preserved mem…

    DOI: 10.1007/s12195-025-00854-1
  4. Ciliated micropillars for the microfluidic-based isolation of nanoscale lipid vesicles Thin

    This study presents a microfluidic device with ciliated micropillars that effectively isolates nanoscale lipid vesicles, such as exosomes, while filtering out larger proteins and cellular debris, allowing for the recovery of intact vesicles.

    DOI: 10.1039/c3lc41343h
  5. Lipid Nanoparticles Enable mRNA Delivery to Diverse Cell Types of the Inner Retina Thin

    Conventional lipid nanoparticles carrying chemically modified mRNA transfect a broader range of inner-retina cell types than previously thought, with subretinal delivery showing higher transfection efficiency than intravitreal delivery, and retinal degeneration (rd1) increasing …

    DOI: 10.1101/2025.11.21.689792
  6. Custom-made lipid nanotubes as a tissue and hydrogel adhesive Colloids and Surfaces A: Physicochemical and Engineering Aspects (2021) Thin

    This study introduces lipid-based AQua nanotube dispersions as adhesives to bond PDMA hydrogels to each other and to soft calf liver tissues, demonstrates superior adhesion compared with silica and solid lipid nanoparticles, analyzes how overlap area, nanotube concentration, and…

    DOI: 10.1016/j.colsurfa.2020.125609
  7. Dual centrifugation – a novel perspective on lipid nanoparticle formulation development RSC Pharmaceutics (2026) Thin

    Downscaled dual centrifugation enables fast, cost-efficient production of miRNA- and mRNA-loaded lipid nanoparticles (LNPs) in 1 mg batches, optimized by a Box-Behnken design to achieve sub-200 nm particles with high encapsulation and potent in vitro transfection while avoiding …

    DOI: 10.1039/d5pm00287g
  8. Anti-melanotransferrin and apolipoprotein E on doxorubicin-loaded cationic solid lipid nanoparticles for pharmacotherapy of glioblastoma multiforme Journal of the Taiwan Institute of Chemical Engineers (2017) Thin

    The study reports the design and in vitro evaluation of doxorubicin-loaded cationic solid lipid nanoparticles grafted with anti-melanotransferrin and apolipoprotein E to cross the blood–brain barrier and suppress glioblastoma cell growth, showing dual-targeting enhances BBB perm…

    DOI: 10.1016/j.jtice.2017.04.026
  9. Preparation and characterization of amorphous amphotericin B nanoparticles for oral administration through liquid antisolvent precipitation European Journal of Pharmaceutical Sciences (2014) Thin

    The study reports the preparation of amorphous amphotericin B nanoparticles via liquid antisolvent precipitation (LAP) followed by freeze-drying, optimization of processing parameters, comprehensive physicochemical characterization, and demonstration of significantly improved di…

    DOI: 10.1016/j.ejps.2013.12.005
  10. Nebulizing novel multifunctional nanovesicles: the impact of macrophage-targeted-pH-sensitive archaeosomes on a pulmonary surfactant J. Mater. Chem. B (2017) Thin

    This study demonstrates that nebulized, macrophage-targeted, pH-sensitive archaeosome nanovesicles (ApH) can cross a pulmonary surfactant monolayer and deliver cytoplasmic cargo to underlying J774A.1 macrophages in vitro, while enhancing surfactant surface activity without causi…

    DOI: 10.1039/c7tb01694h
  11. A multivalent peptide-polymer conjugate material mimics STING to therapeutically activate innate immune signaling Thin

    High-valency display of the STING C-terminal tail on a polymer backbone, delivered by lipid nanoparticles, activates TBK1 and IRF3 signaling to trigger IRF3/NF-κB–driven innate immunity and shrink metastatic ovarian tumors—including in STING-deficient cells—with enhanced efficac…

    DOI: 10.64898/2026.03.24.712780
  12. Lipid–MOF Colloidosomes for Multimodal Encapsulation and Environmental Remediation Thin

    A scalable interfacial lipid–MOF assembly yields hollow lipid-MOF colloidosomes that couple a ZIF-8 MOF shell with a co-assembled lipid phase to enable spatial separation of hydrophobic and hydrophilic cargos while rapidly adsorbing dyes and metal ions from water, with potential…

    DOI: 10.64898/2026.03.24.714078
  13. Targeted delivery of cytotoxic proteins via lipid-based nanoparticles to primary Langerhans cells Nanoscale (2025) Thin

    Glycomimetic-ligand–decorated lipid nanoparticles selectively deliver cytotoxic proteins to langerin-expressing Langerhans cells, enabling cytosolic delivery and targeted depletion in vitro and ex vivo.

    DOI: 10.1039/d4nr03638g
  14. Apicobasal transferrin receptor localization and trafficking in brain capillary endothelial cells Fluids and Barriers of the CNS (2023) Thin

    Basal transferrin receptor localization on brain capillary endothelial cells is demonstrated and TfR trafficking across the BBB occurs bi-directionally, revealed by expansion microscopy in an in vitro porcine BBB model, with implications for iron homeostasis and TfR-targeted bra…

    DOI: 10.1186/s12987-022-00404-1
  15. Delivering Antisense Oligonucleotides across the Blood‐Brain Barrier by Tumor Cell‐Derived Small Apoptotic Bodies Advanced Science (2021) Thin

    A tumor cell–derived, antisense oligonucleotide–loaded small apoptotic body (sCAB) platform crosses the blood–brain barrier via CD44v6–mediated transcytosis to deliver TNF-α ASO to brain microglia, reducing neuroinflammation and ameliorating Parkinsonian symptoms in mice.

    DOI: 10.1002/advs.202004929
  16. Charge Conversional Biomimetic Nanocomplexes as a Multifunctional Platform for Boosting Orthotopic Glioblastoma RNAi Therapy Nano Letters (2020) Thin

    The study develops a three-layer charge-conversion biomimetic nanocomplex (Ang-RBCm-CA/siRNA) that long-circulates, crosses the blood-brain barrier, targets orthotopic glioblastoma cells, releases siRNA in a pH-triggered manner to disrupt RBC membrane and enable cytoplasmic RNAi…

    DOI: 10.1021/acs.nanolett.9b04683
  17. Targeted delivery of BACE1 siRNA for synergistic treatment of Alzheimer's disease Translational Neurodegeneration (2025) Thin

    A RVG29-modified PAMAM-PEG dendrimer delivers BACE1 siRNA across the blood–brain barrier to neurons and microglia, achieving BACE1 knockdown, reduced Aβ, enhanced microglial Aβ clearance, and cognitive improvement in an Alzheimer's disease mouse model.

    DOI: 10.1186/s40035-025-00503-7
  18. Bidirectional apical–basal traffic of the cation-independent mannose-6-phosphate receptor in brain endothelial cells Journal of Cerebral Blood Flow & Metabolism (2017) Thin

    The study demonstrates that the cation-independent mannose-6-phosphate receptor (MPR300) is expressed in adult mammalian brain capillary endothelial cells, internalised from both apical and basal membranes via clathrin- and caveolae-associated pathways, trafficked through endoso…

    DOI: 10.1177/0271678x17700665
  19. Metastatic Brain Tumors Disrupt the Blood-Brain Barrier and Alter Lipid Metabolism by Inhibiting Expression of the Endothelial Cell Fatty Acid Transporter Mfsd2a Scientific Reports (2018) Thin

    Brain metastases disrupt the blood-brain barrier by downregulating endothelial MFSD2A, altering DHA transport and lipid metabolism, with astrocyte-derived TGFβ and bFGF signaling governing MFSD2A expression and suggesting DHA-based strategies could limit brain metastatic growth.

    DOI: 10.1038/s41598-018-26636-6
  20. Transcriptional Profiling for Innate Immunity Receptor CD36 in the Regulation of Endothelial Cell Immunity Via Fatty Acid Metabolism JCO Global Oncology (2024) Thin

    CD36 in brain endothelial cells modulates endothelial immunity via fatty acid metabolism, as revealed by in vivo TRAP-RNA-seq profiling in endothelial-cell-specific CD36 knockout mice.

    DOI: 10.1200/go-24-14400
  21. Innate immune responses to Plasmodium falciparum disrupt the blood-brain barrier Thin

    The study demonstrates that innate immune cells activated by Plasmodium falciparum can adhere to a human 3D in vitro blood–brain barrier, triggering endothelial activation and barrier disruption via LFA-1–ICAM-1 interactions and TNF-α/IFN-γ signaling, thereby revealing an immune…

    DOI: 10.1101/2025.10.20.683440
  22. Mesocricetus auratus (Golden Syrian Hamster) Experimental Model of SARS-CoV-2 Infection Reveals That Lung Injury Is Associated with Phenotypic Differences Between SARS-CoV-2 Variants Viruses (2025) Thin

    In golden Syrian hamsters infected with four different SARS-CoV-2 variants, the study reveals variant-specific lung injury linked to endothelial damage and innate immune responses, with Omicron causing milder pathology and A.2/Delta producing more severe injury, alongside notabl…

    DOI: 10.3390/v17081048
  23. Loss of mitochondrial ClpP, Lonp1, and Tfam triggers transcriptional induction of Rnf213, a susceptibility factor for moyamoya disease neurogenetics (2020) Thin

    Loss of mitochondrial ClpP, Lonp1, or TFAM triggers dsRNA-sensing innate immune signaling that upregulates RNF213, a Moyamoya disease susceptibility gene, across multiple cell types, suggesting a mitochondrial-nucleic acid axis linking mitochondrial stress to vascular disease ri…

    DOI: 10.1007/s10048-020-00609-2
  24. Dengue-2 Structural Proteins Associate with Human Proteins to Produce a Coagulation and Innate Immune Response Biased Interactome BMC Infectious Diseases (2011) Thin

    This study identifies 31 human proteins that physically interact with dengue-2 structural proteins (Env, PrM, Cap) using bacterial two-hybrid screens, constructs a dengue–human interactome, and links these interactions to coagulation and innate immune pathways, suggesting dengue…

    DOI: 10.1186/1471-2334-11-34
  25. Encephalitis due to emerging viruses: CNS innate immunity and potential therapeutic targets Journal of Infection (2012) Thin

    A comprehensive review of how emerging neurotropic viruses invade the CNS, how CNS innate immunity (glia and PRRs) detects infection and how viruses counteract interferon signaling, with discussion of therapeutic targets and delivery challenges across the blood–brain barrier, in…

    DOI: 10.1016/j.jinf.2012.03.019
  26. Long-term Air Pollution Exposure Is Associated with Neuroinflammation, an Altered Innate Immune Response, Disruption of the Blood-Brain Barrier, Ultrafine Particulate Deposition, and Accumulation of Amyloid β-42 and α-Synuclein in Children and Young Adults Toxicologic Pathology (2008) Thin

    The study links lifelong exposure to Mexico City air pollution with neuroinflammation, blood–brain barrier disruption, ultrafine particulate deposition, and early Alzheimer’s disease– and Parkinson’s disease–related protein accumulations (Aβ42 and α-synuclein) in brains and peri…

    DOI: 10.1177/0192623307313011
  27. Endothelial TLR4 signaling drives tissue inflammation, Claudin-5 internalization, and vascular barrier breakdown in a mouse model of neonatal meningitis Thin

    Endothelial intrinsic TLR4 signaling coordinates leptomeningeal inflammation and Claudin-5 trafficking to drive rapid, reversible vascular barrier breakdown in neonatal meningitis, with endothelial Tlr4 deletion preventing inflammation and permeability changes.

    DOI: 10.64898/2025.12.31.697193
  28. Acetaminophen from liver to brain: New insights into drug pharmacological action and toxicity Pharmacological Research (2016) Thin

    This is a comprehensive review that synthesizes mechanisms of acetaminophen (APAP) hepatotoxicity and emerging evidence for its direct effects in the brain, detailing hepatic metabolic pathways, mitochondrial/oxidative stress, necroptotic signaling, and context-dependent neuropr…

    DOI: 10.1016/j.phrs.2016.02.020
  29. Development of Recombinant Anti-TLR2 Antibodies and PLGA Nanoparticle-based Gene Therapy for the Treatment of Neuropathic Pain Thin

    This study develops recombinant anti-TLR2 antibodies (nanobody nb52, nb52 dimer, scFv33, scFv1) and employs biodegradable PLGA nanoparticles to deliver their genes intrathecally in mouse models of neuropathic and inflammatory pain, achieving long-lasting analgesia and reduced sp…

    DOI: 10.1101/2025.11.13.688281

Your question next

What do you want to know?

No question is too uncomfortable for the evidence. Bring yours.

Ask your question